Therapeutic oligonucleotide (nusinersen) metabolism in cerebrospinal fluid samples of patients with spinal muscular atrophy based on liquid chromatography coupled with mass spectrometry data.

Published

Research record: Therapeutic oligonucleotide (nusinersen) metabolism in cerebrospinal fluid samples of patients with spinal muscular atrophy based on liquid chromatography coupled with mass spectrometry data.

Published in Anal Chim Acta; first publication date 2026-03-26. PMID 41997674.

This literature update records publication metadata from Europe PMC. Consult the original publication for its methods, findings and limitations.

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Source

Compiled from public manufacturer materials and regulatory sources. Not independently verified and not reviewed by a named clinician.

Published

2026-03-26

Updated

2026-10-20

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